Over the past three decades, efforts to improve the results of standard treatment for patients with severe aplastic anemia have been largely unsuccessful. The phase III RACE trial, sponsored by the European Society for Blood and Marrow Transplantation (EBMT), published on January 6, 2022 by the New England Journal of Medicine, now demonstrates that adding eltrombopag to standard immunosuppressive treatment is safe and increases response rates in patients with this rare, yet potentially fatal disease.